University of California, Los Angeles
Dr. Melissa Spencer is Professor of Neurology in the UCLA David Geffen School of Medicine, Neuromuscular Program Director. Her lab is utilizing advanced genetic engineering technology to develop new treatments for Duchenne muscular dystrophy and limb girdle muscular dystrophy. These approaches include CRISPR based gene editing platforms as well as gene replacement therapies. The lab is also interested in defining how the immune system promotes muscular dystrophy and how immune cells respond to AAV exposure. Dr. Spencer serves on the Scientific Advisory Committee for the MDA, PPMD and Coalition to Cure Calpain 3. She was awarded a Presidential Early Career Award for Scientists and Engineers (PECASE) in 2001.